Efficacy of PARP inhibition in Pde6a mutant mouse models for retinitis pigmentosa depends on the quality and composition of individual human mutations

K Jiao, A Sahaboglu, E Zrenner, M Ueffing, P A R Ekström, F Paquet-Durand

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Biochemistry, Genetics and Molecular Biology

Medicine and Dentistry

Pharmacology, Toxicology and Pharmaceutical Science

Neuroscience