Fetal Gene Therapy for Acute Neuronopathic Gaucher Disease

Ahad A. Rahim, Andrew M. Wong, Suzanne M. Buckley, Derralynn A. Hughes, Stefan Karlsson, Jonathan D. Cooper, Adrian J. Thrasher, Atul Mehta, Simon N. Waddington

Research output: Contribution to journalPublished meeting abstractpeer-review

Original languageEnglish
Pages (from-to)S357-S357
JournalMolecular Therapy
Volume17
Publication statusPublished - 2009
Event12th Annual Meeting of the American Society of Gene Therapy - San Diego, CA
Duration: 2009 May 272009 May 30

Subject classification (UKÄ)

  • Medical Genetics and Genomics (including Gene Therapy)

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