Generation of two NAGLU-mutated homozygous cell lines from healthy induced pluripotent stem cells using CRISPR/Cas9 to model Sanfilippo B syndrome

Noelia Benetó, Monica Cozar, Laura Gort, Laura Pacheco, Lluïsa Vilageliu, Daniel Grinberg, Isaac Canals

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Article number101668
JournalStem Cell Research
Volume42
DOIs
Publication statusPublished - 2020

Subject classification (UKÄ)

  • Cell and Molecular Biology

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