Molecular evaluation and vector integration analysis of HCC complicating AAV gene therapy for hemophilia B

Manfred Schmidt, Graham R Foster, Michiel Coppens, Hauke Thomsen, Ricardo E. Dolmetsch, Lisbeth Heijink, Paul E Monahan, Steven Pipe

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)4966-9
JournalBlood Advances
Volume7
Issue number17
DOIs
Publication statusPublished - 2023
Externally publishedYes

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