Preclinical Dose-Escalation Study of Intravitreal AAV-RS1 Gene Therapy in a Mouse Model of X-linked Retinoschisis: Dose-Dependent Expression and Improved Retinal Structure and Function
Ronald A Bush, Yong Zeng, Peter Colosi, Sten Kjellström, Suja Hiriyanna, Camasamudram Vijayasarathy, Maria Santos, Jinbo Li, Zhijian Wu, Paul A Sieving
Research output: Contribution to journal › Article › peer-review
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