Sanfilippo syndrome: Molecular basis, disease models and therapeutic approaches

Biochemistry, Genetics and Molecular Biology

• Heparan Sulfate 100%
• Gene 50%
• Induced Pluripotent Stem Cell 50%
• Lysosome 50%
• Membrane 50%
• Glycosaminoglycan 50%
• Disease Modeling 50%

Neuroscience

• Gene 50%
• Stem Cell 50%
• Lysosome 50%
• Central Nervous System 50%

Pharmacology, Toxicology and Pharmaceutical Science

• Lysosome Storage Disease 50%
• Storage Disease 50%