Molecular Therapy, 1525-0024

Tidskrift

Fler filtreringsmöjligheter
  1. 2018
  2. Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery

    Catherine Cukras, Henry E. Wiley, Brett G. Jeffrey, H. Nida Sen, Amy Turriff, Yong Zeng, Camasamudram Vijayasarathy, Dario Marangoni, Lucia Ziccardi, Sten Kjellstrom, Tae Kwon Park, Suja Hiriyanna, J. Fraser Wright, Peter Colosi, Zhijian Wu, Ronald A. Bush, Lisa L. Wei & Paul A. Sieving, 2018 sep 5, I: Molecular Therapy. 26, 9, s. 2282-2294 13 s.

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  3. 2017
  4. Lentiviral Vectors with Cellular Promoters Correct Anemia and Lethal Bone Marrow Failure in a Mouse Model for Diamond-Blackfan Anemia

    Shubhranshu Debnath, Pekka Jaako, Kavitha Siva, Michael Rothe, Jun Chen, Maria Dahl, H. Bobby Gaspar, Johan Flygare, Axel Schambach & Stefan Karlsson, 2017, I: Molecular Therapy. 25, 8, s. 1805-1814

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  5. 2016
  6. CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells

    Megan D Hoban, Dianne Lumaquin, Caroline Y Kuo, Zulema Romero, Joseph Long, Michelle Ho, Courtney S Young, Michelle Mojadidi, Sorel Fitz-Gibbon, Aaron R Cooper, Georgia R Lill, Fabrizia Urbinati, Beatriz Campo-Fernandez, Carmen Flores Bjurström, Matteo Pellegrini, Roger P Hollis & Donald B Kohn, 2016 sep, I: Molecular Therapy. 24, 9, s. 1561-9 9 s.

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  7. Predictive and prognostic clinical variables in cancer patients treated with adenoviral oncolytic immunotherapy

    K Taipale, I Liikanen, A Koski, R Heiskanen, A Kanerva, O Hemminki, M Oksanen, S Grönberg-Vähä-Koskela, K Hemminki, T Joensuu & A Hemminki, 2016 jul, I: Molecular Therapy. 24, 7, s. 1323–1332

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  8. 2015
  9. Case-control estimation of the impact of oncolytic adenovirus on the survival of patients with refractory solid tumors.

    Anna Kanerva, Anniina Koski, Ilkka Liikanen, Minna Oksanen, Timo Joensuu, Otto Hemminki, Juni Palmgren, Kari Hemminki & Akseli Hemminki, 2015, I: Molecular Therapy. 23, 2, s. 321-329

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  10. Controlled striatal DOPA production from a gene delivery system in a rodent model of Parkinson's disease.

    Erik Cederfjäll, Lauren Broom & Deniz Kirik, 2015, I: Molecular Therapy. 23, 5, s. 896-906

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  11. Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.

    Maria Dahl, Alexander Doyle, Karin Olsson, Jan-Eric Månsson, André R A Marques, Mina Mirzaian, Johannes M Aerts, Mats Ehinger, Michael Rothe, Ute Modlich, Axel Schambach & Stefan Karlsson, 2015, I: Molecular Therapy. 23, 5, s. 835-844

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  12. 2013
  13. Functional Neuroprotection and Efficient Regulation of GDNF Using Destabilizing Domains in a Rodent Model of Parkinson's Disease

    Luis Quintino, Giuseppe Manfre, Erika Elgstrand, Angrit Namislo, Christina Isaksson & Cecilia Lundberg, 2013, I: Molecular Therapy. 21, 12, s. 2169-2180

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  14. 2012
  15. Thymic gene transfer of myelin oligodendrocyte glycoprotein ameliorates the onset but not the progression of autoimmune demyelination

    Christopher Siatskas, Natalie Seach, Guizhi Sun, Ashley Emerson-Webber, Aude Silvain, Ban-Hock Toh, Frank Alderuccio, B Thomas Bäckström, Richard L Boyd & Claude C Bernard, 2012 jul, I: Molecular Therapy. 20, 7, s. 1349-59

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  16. 2010
  17. Differential Transduction Following Basal Ganglia Administration of Distinct Pseudotyped AAV Capsid Serotypes in Nonhuman Primates

    Hemraj B. Dodiya, Tomas Björklund, James, III Stansell, Ronald J. Mandel, Deniz Kirik & Jeffrey H. Kordower, 2010, I: Molecular Therapy. 18, 3, s. 579-587

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  18. Successful Treatment of Metachromatic Leukodystrophy Using Bone Marrow Transplantation of HoxB4 Overexpressing Cells

    Noriko Miyake, Koichi Miyake, Stefan Karlsson & Takashi Shimada, 2010, I: Molecular Therapy. 18, 7, s. 1373-1378

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  19. Toward Brain Tumor Gene Therapy Using Multipotent Mesenchymal Stromal Cell Vectors.

    Daniel Bexell, Stefan Scheding & Johan Bengzon, 2010, I: Molecular Therapy. May 4, s. 1067-1075

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  20. 2009
  21. A Recombinant Adenovirus Type 35 Fiber Knob Protein Sensitizes Lymphoma Cells to Rituximab Therapy

    Hongjie Wang, Ying Liu, Zongyi Li, Xiaolong Fan, Akseli Hemminki & Andre Lieber, 2009, I: Molecular Therapy. 17, s. 240

    Forskningsoutput: TidskriftsbidragPublicerat konferensabstract

  22. Bone Marrow Multipotent Mesenchymal Stroma Cells Act as Pericyte-like Migratory Vehicles in Experimental Gliomas.

    Daniel Bexell, Salina Gunnarsson, Ariane Tormin, Anna Darabi, David Gisselsson Nord, Laurent Roybon, Stefan Scheding & Johan Bengzon, 2009, I: Molecular Therapy. 2008, Nov 4., s. 183-190

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  23. Dose Optimization for Long-term rAAV-mediated RNA Interference in the Nigrostriatal Projection Neurons.

    Ayse Ulusoy, Gurdal Sahin, Tomas Björklund, Patrick Aebischer & Deniz Kirik, 2009, I: Molecular Therapy. 17, s. 1574-1584

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  24. Fetal Gene Therapy for Acute Neuronopathic Gaucher Disease

    Ahad A. Rahim, Andrew M. Wong, Suzanne M. Buckley, Derralynn A. Hughes, Stefan Karlsson, Jonathan D. Cooper, Adrian J. Thrasher, Atul Mehta & Simon N. Waddington, 2009, I: Molecular Therapy. 17, s. S357-S357

    Forskningsoutput: TidskriftsbidragPublicerat konferensabstract

  25. Tolerance Induction Using Lentiviral Gene Delivery Delays Onset and Severity of Collagen II Arthritis

    Inger Gjertsson, Karen L. Laurie, James Devitt, Steven J. Howe, Adrian J. Thrasher, Rikard Holmdahl & Kenth Gustafsson, 2009, I: Molecular Therapy. 17, 4, s. 632-640

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  26. 2007
  27. Seizure Suppression by GDNF Gene Therapy in Animal Models of Epilepsy.

    Irene Kanter Schlifke, Biljana Georgievska, Deniz Kirik & Merab Kokaia, 2007, I: Molecular Therapy. 15, s. 1106-1113

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  28. 2006
  29. Lentiviral Vectors for Use in the Central Nervous System.

    Johan Jakobsson & Cecilia Lundberg, 2006, I: Molecular Therapy. 13, 3, s. 484-493

    Forskningsoutput: TidskriftsbidragÖversiktsartikel

  30. Reversal of neurochemical changes and pain-related behavior in a model of neuropathic pain using modified lentiviral vectors expressing GDNF

    S Pezet, A Krzyzanowska, LF Wong, J Grist, ND Mazarakis, Biljana Georgievska & SB McMahon, 2006, I: Molecular Therapy. 13, 6, s. 1101-1109

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  31. 2005
  32. Development of cellular models for ribosomal protein S19 (RPS19)-deficient diamond-blackfan anemia using inducible expression of siRNA against RPS19.

    Koichi Miyake, Johan Flygare, Thomas Kiefer, Taiju Utsugisawa, Johan Richter, Zhi Ma, Maciej Wiznerowicz, Didier Trono & Stefan Karlsson, 2005, I: Molecular Therapy. 11, 4, s. 627-637

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  33. Gene Transfer to Repopulating Human CD34(+) Cells Using Amphotropic-, GALV-, or RD114-Pseudotyped HIV-1-Based Vectors from Stable Producer Cells.

    Thomas Relander, Maria Askmyr, Karin Olsson, Yasuhiro Ikeda, Yasuhiro Takeuchi, Mary Collins & Johan Richter, 2005, I: Molecular Therapy. 11, 3, s. 452-459

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  34. 2004
  35. Chance or necessity? Insertional mutagenesis in gene therapy and its consequences

    C Baum, C von Kalle, F J T Staal, Z X Li, B Fehse, M Schmidt, F Weerkamp, Stefan Karlsson, G Wagemaker & D A Williams, 2004, I: Molecular Therapy. 9, 1, s. 5-13

    Forskningsoutput: TidskriftsbidragÖversiktsartikel

  36. 2003
  37. Enforced adenoviral vector-mediated expression of HOXB4 in human umbilical cord blood CD34+ cells promotes myeloid differentiation but not proliferation.

    Ann Brun, Xiaolong Fan, Jon Mar Björnsson, Keith Humphries & Stefan Karlsson, 2003, I: Molecular Therapy. 8, 4, s. 618-628

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  38. Proliferation deficiency of multipotent hematopoietic progenitors in ribosomal protein S19 (RPS19)-deficient Diamond-Blackfan anemia improves following RPS19 gene transfer

    Isao Hamaguchi, Johan Flygare, Hiroshi Nishiura, Ann Brun, Andreas Ooka, Thomas Kiefer, Zhi Ma, N Dahl, Johan Richter & Stefan Karlsson, 2003, I: Molecular Therapy. 7, 5, s. 613-622

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift

  39. 2002
  40. Overexpression of Gibbon Ape Leukemia Virus (GALV) Receptor (GLVR1) on Human CD34(+) Cells Increases Gene Transfer Mediated by GALV Pseudotyped Vectors.

    Thomas Relander, Ann Brun, Karin Olsson, Lene Pedersen & Johan Richter, 2002, I: Molecular Therapy. 6, 3, s. 400-406

    Forskningsoutput: TidskriftsbidragArtikel i vetenskaplig tidskrift