Neuronal and Astrocytic Differentiation from Sanfilippo C Syndrome iPSCs for Disease Modeling and Drug Development

Noelia Benetó, Monica Cozar, Laura Castilla-Vallmanya, Oskar G Zetterdahl, Madalina Sacultanu, Eulalia Segur-Bailach, María García-Morant, Antonia Ribes, Henrik Ahlenius, Daniel Grinberg, Lluïsa Vilageliu, Isaac Canals

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Medicine and Dentistry

Neuroscience

Biochemistry, Genetics and Molecular Biology

Pharmacology, Toxicology and Pharmaceutical Science