Stable or improved neurological manifestations during miglustat therapy in patients from the international disease registry for Niemann-Pick disease type C: an observational cohort study

Marc C. Patterson, Eugen Mengel, Marie T. Vanier, Barbara Schwierin, Audrey Muller, Peter Cornelisse, Mercè Pineda, NPC Registry investigators

Forskningsoutput: Tidskriftsbidrag › Artikel i vetenskaplig tidskrift › Peer review

Fingeravtryck

Fördjupa i forskningsämnen för ”Stable or improved neurological manifestations during miglustat therapy in patients from the international disease registry for Niemann-Pick disease type C: an observational cohort study”. Tillsammans bildar de ett unikt fingeravtryck.

Medicine and Dentistry